Latest Publications
Liver gene therapy with intein-mediated F8 trans-splicing corrects mouse haemophilia A
Jun 08, 2022EMBO Molecular Medicine
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Liver-Directed Adeno-Associated Virus–Mediated Gene Therapy for Mucopolysaccharidosis Type VI
Jun 06, 2022NEJM Evidence
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The role of NSP6 in the biogenesis of the SARS-CoV-2 replication organelle
May 13, 2022Nature
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Therapeutic homology-independent targeted integration in retina and liver
Apr 12, 2022Nature Communications
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Phosphorylation of FAM134C by CK2 controls starvation-induced ER-phagy
Apr 12, 2022Science Advances
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A single-cell analysis of breast cancer cell lines to study tumour heterogeneity and drug response
Mar 31, 2022Nature Communications
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Modulation of pancreatic cancer cell sensitivity to FOLFIRINOX through microRNA-mediated regulation of DNA damage
Nov 18, 2021Nature Communications
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Comprehensive Analysis of Combinatorial Pharmacological Treatments to Correct Nonsense Mutations in the CFTR Gene
Nov 04, 2021International Journal of Molecular Science
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Correction of oxidative stress enhances enzyme replacement therapy in Pompe disease
Oct 26, 2021Embo Molecular Medicine
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Repurposing of tamoxifen ameliorates CLN3 and CLN7 disease phenotype
Aug 19, 2021EMBO Molecular Medicine
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Single-Cell RNA Sequencing Analysis: A Step-by-Step Overview
Jul 30, 2021RNA Bioinformatics. Methods in Molecular Biology, vol 2284. Humana, New York, NY.
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The Role of MicroRNAs in Mitochondria-Mediated Eye Diseases
Jun 18, 2021Frontiers in Cell and Developmental Biology
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Automatic identification of small molecules that promote cell conversion and reprogramming
May 11, 2021Stem Cell Reports
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Automatic synchronisation of the cell cycle in budding yeast through closed-loop feedback control
Apr 27, 2021Nature Communications
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