1st RNA meeting Mendelian diseases

Sep 05, 2023
1st RNA meeting Mendelian diseases
The first RNA meeting about Mendelian disease starts tomorrow, September 6th, 2023.
The complete scientific program down below.

SCIENTIFIC PROGRAM



8:30 – 8:45 Welcome – Auricchio and Brunetti (TIGEM)

Control of gene expression in Mendelian diseases (Session Chair: Nicola Brunetti)

8:45 – 9:15 Sandro Banfi (TIGEM): “Modulation of microRNA expression: a new therapeutic avenue for inherited retinal disease”
9:15 – 9:45 Alessia Indrieri (TIGEM-IRGB): “Modulation of miR-181a/b as gene-independent therapeutic tool for mitochondrial diseases”
9:45 – 10:15 Elisabetta Tabolacci (UniCatt Rome): “Role of DNMT1 in the epigenetic regulation of the FMR1 gene”
10:15 – 10:45 Coffee break

Novel nucleic acid therapeutics 1 (Session Chair: Alberto Auricchio)

10:45 – 11:15 Gian Gaetano Tartaglia (IIT-Genoa): “Prediction of protein-RNA interactions and applications in neurodegeneration”
11:15 – 11:45 Paloma Giangrande (Wave Therapeutics): “RNA base editing”
11:45 – 12:15 Angela Gallo (IRCCS Bambino Gesù) “Epitranscriptomic crosstalks and cancer cell-killing alternatives”
12:15 – 13:45 LUNCH BREAK

Novel nucleic acid therapeutics 2 (Session Chair: V de Franciscis, Alessia Indrieri)

13:45 – 14:45 Stefano Gustincich (IIT-Genoa) Keynote: “RNA therapeutics for precise targeting”
14:45 – 15:15 Annalisa Di Ruscio (Harvard Medical School): “The hidden avenue of RNA therapeutics in DNA methylation”
15:15 – 15:45 Coffee break
15:45 – 16:15 Velia Siciliano (IIT-Naples): “Regulatory tools for RNA-encoded genetic circuits”

Therapeutic Delivery (Session Chair: Angela Gallo)

16:15 – 16:45 Jeanne Leblond Chain (INSERM Bordeaux) “Aptamer assemblies fortargeting and delivery”
16:45 – 17:15 Pasquale Piccolo (TIGEM): “miRNA-based therapy for liver fibrosis”
17:15 - 17:45 Daniele Catalucci (IRGB): “Inhalable calcium phosphate nanoparticles for the treatment of heart diseases”
17:45 – 18:00 General Discussion and Concluding Remarks Brunetti, Indrieri and V de Franciscis